Postnatal and Prenatal Therapeutic Base Editing for Metabolic Diseases — Kiran Musunuru (CHILDREN'S HOSP OF PHILADELPHIA)
PROJECT SUMMARY The potential for the development of novel therapeutic modalities has energized the genome editing field since it first emerged in the 1990s and especially since the demonstration of p
| Project title | Postnatal and Prenatal Therapeutic Base Editing for Metabolic Diseases |
|---|---|
| Project number | 5U19NS132301-02 |
| PI name | Kiran Musunuru |
| Institution | CHILDREN'S HOSP OF PHILADELPHIA |
| Funding mechanism | U19 |
| Agency | NINDS |
| Award amount | $5.05M |
| Fiscal year | 2024 |
| Project start | 2023-08-01T00:00:00 |
| Project end | 2028-07-31T00:00:00 |
| Abstract | PROJECT SUMMARY The potential for the development of novel therapeutic modalities has energized the genome editing field since it first emerged in the 1990s and especially since the demonstration of p |
| Key terms | <1H-Purin-6-amine><AAV vector><AAV-based vector><ANGPT5><ANGPTL3><ANGPTL3 gene><Address><Adenine><Ad |
$799/mo
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